- Gene Therapy - Human Genome Project - Definition, hurdles, ethical issues, and links to more resources on gene therapy provided by the Oak Ridge National Laboratory.
- Gene Therapy Advisory Committee - GTAC - Advises on the ethical acceptability of proposals for gene therapy research on humans taking account of the scientific merits and the potential benefits and risks, and provides advice to UK Health Ministers on developments in gene therapy research.
- Gene Therapy and Your Child - Development information for the clinical use of gene therapy for children with severe illnesses.
- Gene Therapy Clinical Trials Worldwide - Comprehensive source of information on worldwide gene therapy clinical trials compiled by The Journal of Gene Medicine.
- Harvard Gene Therapy Initiative - Provides plasmid construction and virus production services for gene therapy in both research and therapeutic applications.
- Jesse's Journey - The Foundation for Gene and Cell Therapy - A registered charitable organization raising funds for research in gene and cell based therapies focusing on Duchenne muscular dystrophy and other neuromuscular diseases.
- Office of Biotechnology Activities at the NIH - Monitors scientific progress and ethical issues in basic and clinical research involving recombinant DNA and human gene transfer at NIH funded institutions.
- UK Cystic Fibrosis Gene Therapy Consortium - A consortium whose aims are to provide cystic fibrosis gene therapy updates to researchers, medics, patients and their families.